Rare Genetic Diseases

Rare Genetic Diseases Programs


Congenital Disorders of Glycosylation (CDG)

  • AVTX-801, a therapeutic dose of monosaccharide therapy for PGM1-CDG, an ultra-rare CDG Learn More >
  • AVTX-803, a therapeutic dose of monosaccharide therapy for LAD II, an ultra-rare CDG Learn More >