Rare Genetic Diseases
Rare Genetic Diseases Programs
Congenital Disorders of Glycosylation (CDG)
- AVTX-803, a therapeutic dose of monosaccharide therapy for LAD II, an ultra-rare CDG Learn More >
- AVTX-801, a therapeutic dose of monosaccharide therapy for PGM1-CDG, an ultra-rare CDG Learn More >